Gene therapy works by modifying genetic material to treat disorders, rather than relying on the use of drugs or surgery. Developments in gene therapy are key in the battle against inherited disorders, cancer, AIDS, and many other diseases. Decades worth of advances, including the development of nucleic acid-based therapies, are building a growing number of successful clinical trials and are paving the way for future innovations. In this course, you’ll learn about the fundamentals of gene therapy, the current research and trends in the field, and how it can be applied to improve the health and wellbeing of populations.

  • Edit human genomes to make changes to original DNA
  • Produce genetically modified cells
  • Transfer DNA using Adeno Associated viruses and nanoparticles
  • Regulate genes to treat diseases using RNAi and expression of non-coding RNA
  • Understand the challenges of analyzing big data